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Venglustat combined with imiglucerase for neurological disease in adults with Gaucher disease type 3: the LEAP trial. (2023)

First Author: Schiffmann R

Attributed to: Predictive measures to stratify clinical outcomes in children and adults with Gaucher disease and responses to specific therapies funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.17863/cam.90149

Publication URI: https://www.repository.cam.ac.uk/handle/1810/342736

Type: Journal Article/Review