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Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease. (2024)

First Author: Massaro G

Attributed to: The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/hmg/ddae081

PubMed Identifier: 38757200

Publication URI: http://europepmc.org/abstract/MED/38757200

Type: Journal Article/Review

Volume: 33

Parent Publication: Human molecular genetics

Issue: 17

ISSN: 0964-6906