Comparison of different promoters to improve AAV vector-mediated gene therapy for neuronopathic Gaucher disease. (2024)

First Author: Massaro G

Attributed to: Gene therapy for CLN5 Batten disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/hmg/ddae081

PubMed Identifier: 38757200

Publication URI: http://europepmc.org/abstract/MED/38757200

Type: Journal Article/Review

Parent Publication: Human molecular genetics

ISSN: 0964-6906