Neurodevelopmental and synaptic defects in DNAJC6 parkinsonism, amenable to gene therapy. (2024)
Attributed to:
EnCRISPrx - A Permanent CRISPR-based Approach To Rescue Dravet Syndrome By Enhancing Scn1a Promoter Activity
funded by
MRC
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1093/brain/awae020
PubMed Identifier: 38242634
Publication URI: http://europepmc.org/abstract/MED/38242634
Type: Journal Article/Review
Volume: 147
Parent Publication: Brain : a journal of neurology
Issue: 6
ISSN: 0006-8950