Patient-reported outcomes and measures are under-utilised in advanced therapy medicinal products trials for orphan conditions (2025)
Abstract
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Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.jclinepi.2024.111617
Publication URI: http://dx.doi.org/10.1016/j.jclinepi.2024.111617
Type: Journal Article/Review
Parent Publication: Journal of Clinical Epidemiology