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Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy. (2020)

First Author: Yoon SY
Attributed to:  The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/brain/awaa161

PubMed Identifier: 32671406

Publication URI: http://europepmc.org/abstract/MED/32671406

Type: Journal Article/Review

Volume: 143

Parent Publication: Brain : a journal of neurology

Issue: 7

ISSN: 0006-8950