Global CNS correction in a large brain model of human alpha-mannosidosis by intravascular gene therapy. (2020)
Abstract
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Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1093/brain/awaa161
PubMed Identifier: 32671406
Publication URI: http://europepmc.org/abstract/MED/32671406
Type: Journal Article/Review
Volume: 143
Parent Publication: Brain : a journal of neurology
Issue: 7
ISSN: 0006-8950