Patient-reported outcomes and measures are under-utilised in advanced therapy medicinal products trials for orphan conditions. (2024)
Abstract
No abstract provided
Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.jclinepi.2024.111617
PubMed Identifier: 39608663
Publication URI: http://europepmc.org/abstract/MED/39608663
Type: Journal Article/Review
Volume: 178
Parent Publication: Journal of clinical epidemiology
ISSN: 0895-4356