Sodium valproate, a potential repurposed treatment for the neurodegeneration in Wolfram syndrome (TREATWOLFRAM): trial protocol for a pivotal multicentre, randomised double-blind controlled trial. (2025)
Abstract
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Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1136/bmjopen-2024-091495
PubMed Identifier: 40010822
Publication URI: http://europepmc.org/abstract/MED/40010822
Type: Journal Article/Review
Volume: 15
Parent Publication: BMJ open
Issue: 2
ISSN: 2044-6055