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Optimizing rare disorder trials: a phase 1a/1b randomized study of KL1333 in adults with mitochondrial disease. (2025)

First Author: Pizzamiglio C

Attributed to: MRC Strategic Award to establish an International Centre for Genomic Medicine in Neuromuscular Diseases funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1093/brain/awae308

PubMed Identifier: 39657714

Publication URI: http://europepmc.org/abstract/MED/39657714

Type: Journal Article/Review

Volume: 148

Parent Publication: Brain : a journal of neurology

Issue: 1

ISSN: 0006-8950