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Gene therapy in children with AIPL1-associated severe retinal dystrophy: an open-label, first-in-human interventional study. (2025)

First Author: Michaelides M

Attributed to: Novel therapeutic approaches to rescue retinal dysfunction in patient-derived photoreceptors funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/s0140-6736(24)02812-5

PubMed Identifier: 39986747

Publication URI: http://europepmc.org/abstract/MED/39986747

Type: Journal Article/Review

Volume: 405

Parent Publication: Lancet (London, England)

Issue: 10479

ISSN: 0140-6736