Treating Niemann-Pick C lysosomal storage: approved and emerging approaches (2025)
Abstract
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Bibliographic Information
Digital Object Identifier: http://dx.doi.org/10.1016/j.molmed.2024.11.011
Publication URI: http://dx.doi.org/10.1016/j.molmed.2024.11.011
Type: Journal Article/Review
Parent Publication: Trends in Molecular Medicine
Issue: 2