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Genetic therapies for neurological diseases. (2026)

First Author: Rahim AA

Attributed to: The development of gene therapy for Niemann-Pick type C disease funded by MRC

Abstract

No abstract provided

Bibliographic Information

Digital Object Identifier: http://dx.doi.org/10.1016/j.pharmr.2025.100093

PubMed Identifier: 41389437

Publication URI: http://europepmc.org/abstract/MED/41389437

Type: Journal Article/Review

Volume: 78

Parent Publication: Pharmacological reviews

Issue: 1

ISSN: 0031-6997